Monitoring must continues on gene therapy, possible risks

In order to introduce DNA into cells, gene therapy  uses viruses, but now experimental studies in animals have suggested that when high doses of viruses are used, the process is not as safe as believed. Recent experiments conducted by James Wilson at the University of...

First treatment using gene therapy, to children and adults, approved in the United States

The first treatment using gene therapy is for a serious genetic disease -Inherited Retinal Dystrophy (RD) -that causes vision loss and even blindness. The drug used is called Voretigene neparvovec-rzyl, commercial name LUXTURNA, and is indicated for patients who present with...